United to Beat Time

Action Duchenne, Alex's Wish, Charley's Fund, Coalition Duchenne, Duchenne Foundation, Duchenne Ireland, Duchenne Now, Foundation for a Future, Foundation For Their Sake, Foundation to Eradicate Duchenne, Harrison's Fund, Hope for Gus, Hope for Javier, JB's Keys, Jett Foundation, John Owen's Adventure, Inc (JOA), Joining Jack, Liam's Leep, Little Hercules Foundation, Michael's Cause, Misko Foundation, Muscular Dystrophy Australia, Muscular Dystrophy Foundation India, Nash Avery Foundation, Pietro's Fight, RaceMD, Rally for Ryan, Romito Foundation, Ryan's Quest, Suneels Light, Team Joseph, Team Saij, The Duchenne Children's Trust, The Duchenne Research Fund, Two Smiles One Hope Foundation, Zack Heger Foundation, Zubin's Wish


United to Advance Therapies

CategoryProjectRecipientAffiliationCostPledgedReceivedDisbursedDonate

 
Clinical Trials Travel Grant for REVERSE-DBMD Trial Kathryn Wagner, MD,PhD Kennedy Krieger Institute, Johns Hopkins School of Medicine $25,000 $25,000 $25,000 $25,000

 
Clinical Trials DEXA Clinical Study Elise Townsend, DPT, PhD PCS and Craig Canapari, MD The Pediatric Neuromuscular Clinic at MassGeneral Hospital for Children $10,000 $10,000 $10,000 $10,000

 
Preclinical Therapeutics The Effects of Poloxamer-188 (Carmeseal) on Cardiac and Skeletal Muscle Function in 1-Year Old mdx Mice. Bruce Markham, CSO Phrixus Pharmaceuticals Inc. $67,374 $67,374 $67,374 $67,374

 
Clinical Therapeutics Preparation of the anti-fibrotic halofuginone for use in amulti-center Phase II clinical trial Marc Blaustein, CEO Halo Therapeutics $1,548,000 $1,561,362 $1,548,000 $1,548,000

 
Preclinical Therapeutics Development of dystrophin independent therapy for DMD Louis Kunkel, PhD Boston Children's Hospital $216,762 $216,762 $190,000 $216,762

 
Preclinical Therapeutics Muscle function for candidate compounds Dawn Lowe, PhD University of Minnesota $117,765 $87,500 $85,000 $110,072

 
Preclinical Therapeutics Measurement of in vivo respiratory and cardiac function during dietary enrichment with a nutraceutical in animal models of DMD Joshua Selsby, PhD Iowa State University $206,458 $206,459 $149,500 $206,458

 
Preclinical Therapeutics Antifibrotic Agent for Treatment of Duchenne Muscular Dystrophy Jeffrey Chamberlain, PhD University of Washington $169,528 $147,500 $102,500 $93,743

 
Clinical Trials A Phase I/II Clinical Program to Evaluate HT-100 in DMD Marc Blaustein, CEO Halo Therapeutics $2,400,712 $1,937,000 $1,180,000 $1,085,000

 
Preclinical Therapeutics Determining the mechanisms whereby a nutraceutical enriched diet interrupts disease processes in DMD Joshua Selsby, PhD Iowa State University $232,171 $97,500 $85,000 $15,000

 
Clinical Therapeutics Moving Carmeseal-MD into the clinic to treat respiratory and cardiac dysfunction in non-ambulatory Duchenne muscular dystrophy patients Bruce Markham, CSO Phrixus Pharmaceuticals Inc. $130,488 $25,000 $0 $0

 
Clinical Trials ISOFEN, multi-cener clinical trial in DMD Emilio Clementi, MD University of Milano $1,485,117 $1,318,302 $638,302 $0